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A Centralized Platform study for Functional High Risk Multiple Myeloma: Domain 1

ACTRN 12625000438459

Brief Summary

The purpose of this platform study is to assess the efficacy of teclistamab and talquetamab for patients who have functional high-risk disease, defined as relapsing or refractory within 18 months of first-line myeloma treatment. Patients who have functional high-risk disease currently do not have optimal treatments available via the Pharmaceutical Benefits Scheme and have poorer outcomes compared to myeloma patients who are not considered functional high-risk.

Intervention/Treatment

  • Drug: Talquetamab
  • Drug: Teclistamab

Inclusion Criteria:

  • Age >= 18 years of age.
  • Able to provide written consent.
  • Documented diagnosis of MM with measurable disease as define by any of the following
  • Serum M-component greater than 5 g per L and/or
  • Urine M-component greater than200 mg per 24 h, and/or
  • Involved serum free light chain level greater than 100mg per L.
  • Patients who do not meet these criteria but have biopsy proven extra-medullary disease (extra-osseous plasmacytoma that is not contiguous with an osseous plasmacytoma) that can undergo response evaluation with serial PET-CT are considered to have measurable disease.
  • Documented evidence of progressive disease within 18 months of commencing front-line therapy for newly diagnosed MM according to IMWG response criteria
  • Patients must have received only 1 prior therapy consisting of an IMID or PI-based induction regimen with or without high dose melphalan conditioned autologous stem cell transplant +/- lenalidomide maintenance.
  • No contraindication to the use of any of the study drugs and able to comply with trial requirements.
  • Adequate liver function (total bilirubin less than 2.0x upper limit of normal (ULN), alanine aminotransferase less than 5.0x ULN) unless considered secondary to MM.
  • Absolute neutrophil count greater than or equal to 1.0 x 10^9 per L. Granulocyte colony-stimulating factor (G-CSF) therapy is permitted on study.
  • Platelet count greater than or equal to 50 x 10^9 per L (greater than or equal to 30 x 10^9 per L if MM involvement in the marrow is greater than 50 per cent), patients should not have received platelet transfusions within 7 days of the screening platelet count.
  • Hb greater than or equal to 80 g per L, red cell transfusions as per institutional protocol are allowed.
  • Has provided written informed consent.
  • Women of childbearing potential participants must not become pregnant while on study; male participants must not father children while on study

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