Rhabdoid Tumours

Rhabdoid tumours, commonly referred to as malignant rhabdoid tumours, are rare malignancies that generally affect young children. In most cases they develop in the kidneys or the brain/central nervous system, however it can less commonly develop in other areas of the body, including soft tissues, lung, skin. 

Rhabdoid tumours that develop in the brain or CNS are called Atypical Teratoid/Rhabdoid tumours (ATRT), and are classified as a type of embryonal tumour. For more information on ATRTs and embryonal tumours, please refer to the Rare Cancers Australia Embryonal Tumours page. 

Rhabdoid tumours are slightly more common in males, and tend to be diagnosed under the age of two. However, anyone can develop this disease. 

Treatment

If a rhabdoid tumour is detected, it will be staged and graded based on size, metastasis, and how the cancer cells look under the microscope. Staging and grading helps your doctors determine the best treatment for you.  

Cancers can be staged using the TNM staging system:

  • T (tumour) indicates the size and depth of the tumour.
  • N (node) indicates whether the cancer has spread to nearby lymph nodes.
  • M (metastasis) indicates whether the cancer has spread to other parts of the body.

This system can also be used in combination with a numerical value, from stage 0-IV:

  • Stage 0: this stage describes cancer cells in the place of origin (or ‘in situ’) that have not spread to nearby tissue.
  • Stage I: cancer cells have begun to spread to nearby tissue. It is not deeply embedded into nearby tissue and had not spread to lymph nodes. This stage is also known as early-stage cancer.
  • Stage II: cancer cells have grown deeper into nearby tissue. Lymph nodes may or may not be affected. This is also known as localised cancer.
  • Stage III: the cancer has become larger and has grown deeper into nearby tissue. Lymph nodes are generally affected at this stage. This is also known as localised cancer.
  • Stage IV: the cancer has spread to other tissues and organs in the body. This is also known as advanced or metastatic cancer.

Cancers can also be graded based on the rate of growth and how likely they are to spread:

  • Grade I: cancer cells present as slightly abnormal and are usually slow growing. This is also known as a low-grade tumour.
  • Grade II: cancer cells present as abnormal and grow faster than grade-I tumours. This is also known as an intermediate-grade tumour.
  • Grade III: cancer cells present as very abnormal and grow quickly. This is also known as a high-grade tumour.

Once your tumour has been staged and graded, your doctor may recommend genetic testing, which analyses your tumour DNA and can help determine which treatment has the greatest chance of success. They will then discuss the most appropriate treatment option for you.

Treatment is dependent on several factors, including location, stage of disease and overall health.

Treatment options for rhabdoid tumours may include:

  • Surgery to remove as much of the tumour(s) as possible – varies based on tumour location(s). 
  • Chemotherapy. 
  • Radiation therapy. 
  • Stem cell transplant. 
  • Clinical trials. 
  • Palliative care. 

Risk factors

While the cause of rhabdoid tumours remains unknown, some of the following factors may increase the likelihood of developing the disease: 

  • Genetic mutations of the SMARCB1 gene. 
  • Having rhabdoid tumour predisposition syndrome (RTPS). 

Not everyone with these risk factors will develop the disease, and some people who have the disease may have none of these risk factors. See your general practitioner (GP) if you are concerned. 

Symptoms

The symptoms of rhabdoid tumours will often vary based on location. 

Symptoms of Rhabdoid Tumours in the Kidney 

Symptoms of rhabdoid tumours in the kidneys may include: 

  • Abdominal mass 
  • Hypertension.
  • Haematuria.
  • Hypercalcaemia.  
  • Difficulty urinating. 

Symptoms of Atypical Teratoid/Rhabdoid Tumours 

Symptoms of ATRTs may include: 

  • Difficulties with balancing and coordination and/or walking. 
  • Slowed speech.  
  • Headache, especially in the morning. 
  • Headache that only goes away after vomiting. 
  • General weakness and fatigue. 
  • Seizures. 
  • Diplopsia and/or other eye problems. 
  • Nausea and/or vomiting. 
  • Irritability. 
  • Slowed growth. 
  • Changes in eating habits. 
  • Delayed developmental milestones, such as sitting up, walking and talking. 

Not everyone with the symptoms above will have cancer, but see your general practitioner (GP) if you are concerned.  

Diagnosis

If your doctor suspects you have a rhabdoid tumour, they may order the following tests to confirm the diagnosis and refer you to a specialist for treatment:

  • Physical examination.
  • Neurological examination.
  • Blood tests.
  • Urine tests.
  • Imaging tests, potentially including:
    • MRI (magnetic resonance imaging).
    • CT (computed tomography) scan.
    • PET (positron emission tomography) scan.
    • Ultrasound.
    • Bone scan.
  • Exploratory surgery, potentially including:
    • Cystoscopy.
    • Ureteroscopy.
    • Bronchoscopy.
    • Mediastinoscopy.
    • Thoracoscopy.
  • Biopsy.

References

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